Although juvenile Batten disease was first described more than 200 years ago, it wasn’t until 1995 when the genetic culprit, the CLN3 gene, was identified that investigators were able to pinpoint the exact cause of the disease. By the late 1990s, rapid technological advances in the development of small animal models, light microscopy, array technology and other techniques helped investigators add significant knowledge to our understanding of the disease.

In order to translate these discoveries into therapies, BBDF has created a cohesive strategy that identifies and prioritizes knowledge gaps and action items in the pathway from here to a cure and is executing an efficient plan towards treatment for this disease. Watch the video to see how BBDF is working with research institutions, the pharmaceutical industry, and government agencies to cross the “Valley of Death” between initial scientific discoveries and meaningful progress towards a cure.

Our Partners

Our combined objectives are to prevent, diagnose, treat and cure juvenile Batten disease. To achieve these goals, we are engaged in multiple partnership activities with other affected families, Batten disease nonprofits, research institutes, government advisories, Pharmaceutical companies, regulatory experts and high-profile foundations committed to fighting neurodegenerative diseases

Read More »

300acfnlogo   abbvie-logo-eps-vector-image   ALBERT EINSTEIN COLLEGE OF MEDICINE LOGO   addf_logo_web  aan-logo    abf-logo-color    AbD    lpamicus  bdfa-logo2  battendisease_supportandresearch bcm_logoPicture-35-Biomarin-logo  bio-logo    blakes-purpose  brightfocus_foundation_logo   catherineshopeforacure   Children's Tumor Foundation contactpunt   cureswithinreach dana_foundation logo-devcelldynlab1  Drew's Hope embo-logo-20123embo evelina  everylife-logo   evotec  exemplar  exlpharma    Faster Cures    faseb-logo fda-logo  gabo  genentech-logo-750  genes-devgenome-research  genzyme-logo-svg  grc  krieger-small-vertical-blue-500px  junicon  hndc_new_logo_without_background Print  haydens-hope  hcm-strategists-logo  Logo_Color_Full  human-molecular-genetics  screen-shot-2016-10-10-at-11-03-33-am  jasperagainstbatten  jonahsjustbegun  kings_college_london_uk_logo  krames    lrbf  mgh-clear-background-large  mrcg  mjff_new_logo_560nature-cell-biology  ncgr nmss   ncllogo  nyasblg_rgb   nycomps_logo  new_york_stem_cell_logo  noahs-hope_logo-small  orphansolutions  ourpromiseplos-one-logo_large-3s600x600 Rutgers,_The_State_University_of_New_Jersey_logo     sairosefoundation  kompetens-logo_fi  sform1  science-aaas-stacked-color  stm_logo_rgb  taylor_logo_color  teamsanfilippo535d4c7a9862e-5388cbc7c1bdc  logotigem  tchlogo  pgimer-logo  thomsonreuters kmiptbxa  cover_dismissionefacolta    hamburg-eppendorf_logo  ioe_black_small_logo  logo-university_of_iowa  hpt_unc-ch  university-of-rochester-logo umdnj-logo    440px-logo_association_vml    weizmann    zfs_logo  zotero_logo                       

One thought on “Our Strategy

Leave a Reply

Your email address will not be published. Required fields are marked *