Where can I find information about diagnosis or management of CLN3 Batten disease?

The average patient with a rare disease visits 8 physicians and receives 2 to 3 misdiagnoses before being correctly diagnosed. On average, this takes 7.6 years.

In rare and currently incurable diseases like CLN3 disease, the lack of a diagnosis or misdiagnoses increases family stress, is expensive, time-consuming, can result in mistreatment, and prevents access to effective family support services.

If you or your doctor suspect your child has CLN3 disease or another of the 13 forms of Neuronal Ceroid Lipofuscinoses (Batten disease), the institutions listed below provide diagnostic testing, health management, and genetic counseling services for Batten disease across United States.

Batten Disease Support Research and Advocacy (BSDRA) Foundation Centers of Excellence:

Centers of Excellence

Children’s Hospital Colorado (affiliated with the University of Colorado, Denver)

Children’s Hospital of Orange County (CHOC)

Kennedy Krieger Institute

Nationwide Children’s Hospital

NYU Langone Health

University of Rochester Batten Center

Affiliate Centers

Boys Town National Research Hospital

Children’s National Hospital, Washington D.C

C.S. Mott Children’s Hospital at University of Michigan Medicine

Mount Sinai Health System

Rush University Medical Center

Clinical guidelines for CLN3 Batten disease

Recommendations for the diagnosis and management of CLN3 disease (Batten disease) using the Delphi consensus methodology. 

Children’s National Hospital, Washington D.CC.S. Mott Children’s Hospital at University of MichiganMedicineMount Sinai Health SystemRush University Medical CenterClinical guidelines for CLN3 Batten disease.

Jonathan W. Mink, Heather R. Adams, Rebecca Ahrens-Nicklas, Brian Nauheimer Andersen, Erika Augustine, Rose‑Mary Boustany, Jonathan D. Cooper, Alex Levin, Paul Gissen, MinnaLaine, Heather L. Mason, Sara E. Mole, Miriam Nickel, John R. Ostergaard, Lori Sikorra, LaurenTreat, Ineka T. Whiteman, Ruth Williams & Angela Schulz.

Orphanet J Rare Dis(2026).

This project wasproudly supported by funding and in-kind support from the Beyond BattenDisease Foundation, and co-authored by BBDF Principal Scientific Consultant, InekaWhiteman, PhD.

Leave a Reply

Your email address will not be published. Required fields are marked *