10 Jun 2023 Expert Insights on Gene Therapy for International Batten Awareness Day June 10, 2023 BeyondBatten Research, News Neuronal ceroid lipofuscinosis (NCL) is a group of 13 rare inherited lysosomal disorders affecting the ne...Read More
7 Jun 2023 Theranexus and BBDF granted positive opinion by EMA for the design of Phase III trial to evaluate Batten-1 in CLN3 Batten disease June 7, 2023 BeyondBatten Research, News, Press Releases Lyon, France – Austin, Texas, United States – 7 June 2023 – 7.30 am CEST – Theranexus, a biopharmaceutica...Read More
16 May 2023 Families raised millions and handed rare disease therapies off to biotechs. But companies have backed out May 16, 2023 BeyondBatten News When Julia Taravella’s two sons were diagnosed with an ultra-rare disease, she did something extraordinar...Read More
9 May 2023 Theranexus and BBDF win FDA approval on efficacy endpoints for the Phase III trial to evaluate Batten-1 in CLN3 Batten disease May 9, 2023 BeyondBatten Research, News, Press Releases Theranexus and BBDF win FDA approval on efficacy endpoints for the Phase III trial to evaluate Batten-1 i...Read More
2 Mar 2023 My son’s time is running out due to a rare disease. The FDA needs to add more clinical trial flexibility March 2, 2023 BeyondBatten Family Stories By Judy Stecker Feb. 28, 2023 My toddler, Wheeler, will probably not live to adulthood. Juvenile Batten...Read More
26 Feb 2023 BBDF Presents at World Symposia 19th Annual Scientify Meeting February 26, 2023 BeyondBatten Research, News BBDF was proud to partner with Theranexus and Engaged Health to present Understanding the Functional Burd...Read More
23 Feb 2023 Rare Disease Day 2023 – A Discussion February 23, 2023 BeyondBatten Research, News ...Read More
22 Feb 2023 THERANEXUS, BBDF AND CARDIFF UNIVERSITY PRESENT THEIR NOVEL RESEARCH ON BATTEN-1 AND BATTEN DISEASE AT WORLDSYMPOSIUM 2023 February 22, 2023 BeyondBatten Research, News, Press Releases From 22 to 26 February 2023 in Orlando, Florida ▪ Presentation of preclinical data demonstrating how Ba...Read More
6 Feb 2023 NCL Congress Report February 6, 2023 BeyondBatten Research, News BBDF sponsored Ineka Whiteman, PhD to attend the 7th Meeting Translational Research Conference for the Ma...Read More
5 Jan 2023 New Advance to the Theranexus and BBDF Batten-1 Program for Juvenile Batten Disease (CLN3) January 5, 2023 BeyondBatten Research, News, Press Releases Beyond Batten Disease Foundation is excited to share the latest accomplishment on our journey to find a t...Read More